• Infectious diseases, including HIV, influenza, Ebola virus, and Marburg virus

  • Rheumatology, including rheumatoid arthritis, psoriatic arthritis, and ankylosing spondylitis

  • Cystic fibrosis

  • Oncology, including ovarian cancer, lung cancer, multiple myeloma, and head and neck cancer

  • Gene therapy, adeno-associated virus (AAV) in particular

  • Antisense RNA, phosphorodiamidate morpholino oligomers (PMOs) in particular

  • Animal Rule, bridging efficacy in animals and safety in humans to bring drugs to market